what is mps treatment?
Although there is no cure for MPS I, treatments can improve the quality of life -- especially when started early. They slow the disease and help stop damage before it starts. Most kids who have less severe MPS I can go to school with other children.
The study was conducted in mouse models of lysosomal storage disease and in cells from blood samples donated by people with Gaucher disease. Current treatments for Gaucher and other lysosomal storage diseases (LSDs) include enzyme replacement therapy or substrate reduction therapy. These break down or prevent the accumulation of certain fatty molecules and other waste particles that clog cells to cause inflammation, cell and organ damage and, in some cases, death.