It's becoming a reality to correct defective genes in patients with inherited diseases, such as severe combined immunodeficiency, you may know it as the bubble boy syndrome, and sickle cell anemia.
Se está convirtiendo en realidad el corregir los genes defectuosos de pacientes con enfermedades hereditarias como la inmunodeficiencia combinada grave, conocida como síndrome del niño burbuja, o la anemia falciforme.