<unk> , sold under the brand name Voxzogo, is a medication used for the treatment of achondroplasia. The most common side effects include injection site reactions (such as swelling, redness, itching or pain), vomiting and decreased blood pressure. Achondroplasia is a genetic condition that causes severely short stature and disproportionate growth. The average height of an adult with achondroplasia is approximately four feet. People with achondroplasia have a genetic mutation that causes a certain growth regulation gene called fibroblast growth factor receptor 3 to be overly active, which prevents normal bone growth.<unk>  works by binding to a specific receptor called natriuretic peptide receptor-B that reduces the growth regulation gene’s activity and stimulates bone growth.<unk>  was approved for medical use in the European Union in August 2021, and in the United States in November 2021.
Vosoritide
Oprelvekin
Selexipag
Eteplirsen
Ganirelix
Tezacaftor
Ecallantide
Vagisil