<unk> , marketed as Spinraza, is a medication used in treating spinal muscular atrophy (SMA), a rare neuromuscular disorder. In December 2016, it became the first approved drug used in treating this disorder. Since the condition it treats is so rare,<unk>  has so-called “orphan drug” designation in the United States and the European Union.
Nusinersen
Inotersen
Belinostat
Memantine
Glybuzole
Glysobuzole
Ozanimod
Siponimod