From personal genomics to gene therapy The treatment of<unk> s is an ongoing battle, with over 1,800 gene therapy clinical trials having been completed, are ongoing, or have been approved worldwide. Despite this, most treatment options revolve around treating the symptoms of the<unk> s in an attempt to improve patient quality of life. Gene therapy refers to a form of treatment where a healthy gene is introduced to a patient. This should alleviate the defect caused by a faulty gene or slow the progression of the disease. A major obstacle has been the delivery of genes to the appropriate cell, tissue, and organ affected by the<unk> . Researchers have investigated how they can introduce a gene into the potentially trillions of cells that carry the defective copy. Finding an answer to this has been a roadblock between understanding the<unk>  and correcting the<unk> .
Genetic disorder
Degenerative disease
Autoimmune disease
Metabolic disorder
Viral disease
Vascular anomaly
Immune disorder
Neurodegenerative disease