This association at mdausa.org is supporting gene therapy trials to help find a cure
... on finding better 
ways to prevent, treat, and ultimately cure disorders such ... NIH Patient 
Recruitment for Motor Neuron Diseases Clinical Trials ... mda@mdausa.org [DOC] [TLE] Friedreich's Ataxia Fact Sheet [PAR] Friedreich's ataxia is caused by a defect (mutation) in a gene labeled FXN.